Clinical Trial News: Positive results in Usher syndrome and RP clinical study

ProQR news – Positive results achieved in our ongoing Usher syndrome and retinitis pigmentosa research.


Stellar study, Phase 1/2 clinical trial showed investigational RNA therapy QR-421a is effective and safe. ProQR plans to start final phase trials for people with USH2A mediated retinitis pigmentosa.

We are pleased to announce the positive results of our Usher syndrome and retinitis pigmentosa clinical study Stellar, which has met all its stated objectives. This marks a crucial milestone in our ongoing inherited retinal disease research.


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