ProQR seeking Clinical Trial Participants
Usher Syndrome Coalition announces partnership with ProQR to support clinical trial enrollment for a potential therapy for USH2A.
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- Dec 21, 2021
First patients dosed in phase 2/3 gene therapy trial for retinitis pigmentosa
The first patients have been dosed in the phase 2/3 Sirius and Celeste clinical trials investigating QR-421a in patients with USH2A.
- May 23, 2021
Clinical Trial News: Positive results in Usher syndrome and RP clinical study
ProQR news – Positive results achieved in our ongoing Usher syndrome and retinitis pigmentosa research.
- Dec 31, 2019
USH2A Gene in Retinitis Pigmentosa: A Tale of Three Patients
By Patricia C Sanchez Diaz, DVM, PhD, FAAO Purpose This report aims to illustrate the impact of genetic testing in the diagnosis and...
- Apr 21, 2016
Panel-based NGS Reveals Novel Pathogenic Mutations in Autosomal Recessive Retinitis Pigmentosa
Targeted next-generation sequencing (NGS) has been demonstrated to be an effective strategy for the detection of mutations in RP.
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