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![New Gene Therapy for Retinitis Pigmentosa Shows Promise](https://static.wixstatic.com/media/nsplsh_675ad0429fdd419694dc026edb18331a~mv2.jpg/v1/fill/w_292,h_219,fp_0.50_0.50,q_90,enc_auto/nsplsh_675ad0429fdd419694dc026edb18331a~mv2.webp)
Oct 19, 2024
New Gene Therapy for Retinitis Pigmentosa Shows Promise
New research . . . suggests that a new kind of gene therapy can improve vision in people who have lost nearly all sight to RP.
![](https://static.wixstatic.com/media/77bbd3_a9411a3407e04337bf86081dca9cbca8~mv2.jpg/v1/fill/w_250,h_250,fp_0.50_0.50,q_30,blur_30,enc_auto/77bbd3_a9411a3407e04337bf86081dca9cbca8~mv2.webp)
![Gene Therapy Improves Functional Measures in XLRP](https://static.wixstatic.com/media/77bbd3_a9411a3407e04337bf86081dca9cbca8~mv2.jpg/v1/fill/w_292,h_219,fp_0.50_0.50,q_90,enc_auto/77bbd3_a9411a3407e04337bf86081dca9cbca8~mv2.webp)
Mar 13, 2024
Gene Therapy Improves Functional Measures in XLRP
Patients with XLRP treated with AGTC-501 gene therapy experienced improvements in visual function including retinal sensitivity . . .
![](https://static.wixstatic.com/media/nsplsh_746f386f3062714f413651~mv2.jpg/v1/fill/w_250,h_250,fp_0.50_0.50,q_30,blur_30,enc_auto/nsplsh_746f386f3062714f413651~mv2.webp)
![Potential of endogenous regenerative technology for in situ regenerative medicine](https://static.wixstatic.com/media/nsplsh_746f386f3062714f413651~mv2.jpg/v1/fill/w_292,h_219,fp_0.50_0.50,q_90,enc_auto/nsplsh_746f386f3062714f413651~mv2.webp)
Jul 23, 2022
Potential of endogenous regenerative technology for in situ regenerative medicine
Endogenous regenerative technology involves the use of a patient's biologically active proteins, growth factors and biomaterial scaffolds.
![A new hope for a therapy against retinitis pigmentosa](https://static.wixstatic.com/media/77bbd3_d96a30483ad2446ebd0440867cbd6310~mv2.png/v1/fill/w_292,h_219,fp_0.50_0.50,q_95,enc_auto/77bbd3_d96a30483ad2446ebd0440867cbd6310~mv2.webp)
Jun 16, 2022
A new hope for a therapy against retinitis pigmentosa
June 17, 2022 | Université de Genève Journal Reference Olivier Mercey, Corinne Kostic, Eloïse Bertiaux, Alexia Giroud, Yashar Sadian,...
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![Antabuse may help revive vision in people with progressive blinding disorders](https://static.wixstatic.com/media/77bbd3_1b755f59a0b745af961d3f43a0f06c45~mv2.jpeg/v1/fill/w_292,h_219,fp_0.50_0.50,q_90,enc_auto/77bbd3_1b755f59a0b745af961d3f43a0f06c45~mv2.webp)
Mar 17, 2022
Antabuse may help revive vision in people with progressive blinding disorders
UC Berkeley researchers have found that a drug once widely used to wean alcoholics off drinking may help improve sight in mice with RD.
![New Treatments for Retinitis Pigmentosa](https://static.wixstatic.com/media/77bbd3_ee2235cea1e24bbc94a7e4250671df60~mv2.png/v1/fill/w_292,h_219,fp_0.50_0.50,q_95,enc_auto/77bbd3_ee2235cea1e24bbc94a7e4250671df60~mv2.webp)
Aug 15, 2021
New Treatments for Retinitis Pigmentosa
Existing treatments only help a fraction of the estimated 100,000 Americans with this condition. But advances in gene therapy may soon help.
![](https://static.wixstatic.com/media/77bbd3_07488f68c28f4e3881482483351476e9~mv2.jpg/v1/fill/w_250,h_250,fp_0.50_0.50,q_30,blur_30,enc_auto/77bbd3_07488f68c28f4e3881482483351476e9~mv2.webp)
![FDA grants orphan drug designation for RP treatment](https://static.wixstatic.com/media/77bbd3_07488f68c28f4e3881482483351476e9~mv2.jpg/v1/fill/w_292,h_219,fp_0.50_0.50,q_90,enc_auto/77bbd3_07488f68c28f4e3881482483351476e9~mv2.webp)
Mar 15, 2021
FDA grants orphan drug designation for RP treatment
The FDA has granted orphan drug designation for chemically induced photoreceptor-like cells to treat retinitis pigmentosa.
![FDA grants fourth ODD for treatment of PDE6B gene mutation-associated retinal diseases](https://static.wixstatic.com/media/77bbd3_5641d8667f484829ac19838e0d93764e~mv2.png/v1/fill/w_292,h_219,fp_0.50_0.50,q_95,enc_auto/77bbd3_5641d8667f484829ac19838e0d93764e~mv2.webp)
Aug 11, 2020
FDA grants fourth ODD for treatment of PDE6B gene mutation-associated retinal diseases
FDA granted 4th Orphan Drug Designation for novel gene therapy product candidate (OCU400, Ocugen Inc.) in treatment of PDE6B gene mutation.
![Understanding the molecular mechanisms underlying retina degeneration in INPP5E-Joubert Syndrome](https://static.wixstatic.com/media/77bbd3_d4d279ace9284d72bebbfa5c7d3d9874~mv2.png/v1/fill/w_292,h_219,fp_0.50_0.50,q_95,enc_auto/77bbd3_d4d279ace9284d72bebbfa5c7d3d9874~mv2.webp)
Jul 14, 2018
Understanding the molecular mechanisms underlying retina degeneration in INPP5E-Joubert Syndrome
Our goal is to identify the onset of degeneration and devise gene-based therapies to ameliorate or cure the retina disease.
![First Gene Therapy FDA-Approved for an Inherited Retinal Disease](https://static.wixstatic.com/media/77bbd3_d68f9f9884d64404b9eaa87c0eda792b~mv2.png/v1/fill/w_225,h_219,fp_0.50_0.50,q_95,enc_auto/77bbd3_d68f9f9884d64404b9eaa87c0eda792b~mv2.webp)
Mar 31, 2018
First Gene Therapy FDA-Approved for an Inherited Retinal Disease
In 1972, Friedman and Roblin proposed that it was theoretically possible to introduce “good” DNA to replace defective DNA.
![](https://static.wixstatic.com/media/77bbd3_97deb4cf5bd4409fb6492024c4e8d218~mv2.jpg/v1/fill/w_250,h_250,fp_0.50_0.50,q_30,blur_30,enc_auto/77bbd3_97deb4cf5bd4409fb6492024c4e8d218~mv2.webp)
![FDA Approves Gene Therapy for Inherited Blindness Developed by the UPenn and CHOP](https://static.wixstatic.com/media/77bbd3_97deb4cf5bd4409fb6492024c4e8d218~mv2.jpg/v1/fill/w_292,h_219,fp_0.50_0.50,q_90,enc_auto/77bbd3_97deb4cf5bd4409fb6492024c4e8d218~mv2.webp)
Dec 19, 2017
FDA Approves Gene Therapy for Inherited Blindness Developed by the UPenn and CHOP
In 2017, the FDA approved a gene therapy for RP caused by RPE65. The decision marked the first approved treatment for any form RP.
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![Stem Cell Therapy: Novel Approach, RP Vision Restoration](https://static.wixstatic.com/media/77bbd3_561592f7b812409696bb82f2f3e55f9c~mv2.jpg/v1/fill/w_292,h_219,fp_0.50_0.50,q_90,enc_auto/77bbd3_561592f7b812409696bb82f2f3e55f9c~mv2.webp)
Jun 30, 2013
Stem Cell Therapy: Novel Approach, RP Vision Restoration
Medical Hypothesis, Discovery Innovation Ophthalmology Journal | Harvey Siy Uy, MD, Pik Sha Chan, MD, and Franz Marie Cruz, MD | 2013...
![Scientists for the First Time Regenerate Sections of Retinas and Increase Visual Function With Stem](https://static.wixstatic.com/media/77bbd3_698e26dedb7e49bfb9de16a44551bac5~mv2.png/v1/fill/w_292,h_142,fp_0.50_0.50,q_95,enc_auto/77bbd3_698e26dedb7e49bfb9de16a44551bac5~mv2.webp)
May 15, 2011
Scientists for the First Time Regenerate Sections of Retinas and Increase Visual Function With Stem
Fierce Biotech | May 16, 2011, 08:05 am | Boston | PRNewswire-US Newswire Scientists from Schepens Eye Research Institute are the first...
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![Regenerative Therapy for Retinal Disorders](https://static.wixstatic.com/media/nsplsh_08047b4ee9884ab0b473af8336b4ea0c~mv2.jpg/v1/fill/w_292,h_219,fp_0.50_0.50,q_90,enc_auto/nsplsh_08047b4ee9884ab0b473af8336b4ea0c~mv2.webp)
Sep 30, 2010
Regenerative Therapy for Retinal Disorders
Discusses stem cells, dev stages of the eye field, eye field transcriptional factors, and endogenous and exogenous sources of stem cells.
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